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News
Award topping $35M to fuel CHOP gene editing work in hemophilia
1+ day, 11+ hour ago (494+ words) New 5-year funding aims to advance personalized treatments for 4 rare diseases Written by Steve Bryson, PhD | July 24, 2026 Children’s Hospital of Philadelphia (CHOP) has been awarded up to $38.9 million to advance the development of personalized gene‑editing therapies for four groups…...
Many women with hemophilia face heavy symptoms and care gaps
4+ day, 6+ hour ago (904+ words) New review highlights ongoing challenges in diagnosis, treatment Written by Marisa Horak, MS | July 21, 2026 Although it’s often mistakenly thought of as a male disease, hemophilia affects a substantial number of women and girls, manifesting with symptoms that can include heavy…...
Experimental treatment maintains low bleed rates in hemophilia A
1+ week, 1+ day ago (583+ words) Extension study reports reduced treatment burden across dosing schedules Written by Michela Luciano, PhD | July 17, 2026 Denecimig (Mim8), an investigational antibody therapy being developed by Novo Nordisk, continued to maintain low bleeding rates in children, adolescents, and adults with hemophilia A, with…...
Early genetic testing may ensure babies are born hemophilia-free
1+ week, 4+ day ago (844+ words) 10-year study suggests procedure is a 'reliable option' for couples using IVF Written by Michela Luciano, PhD | July 14, 2026 For couples affected by hemophilia who want to avoid passing the inherited bleeding disorder to their children, early genetic testing — done during…...
How hemophilia has changed what I expect from my goals
2+ week, 1+ day ago (587+ words) Goals are now like infrastructure, systems that support the life I'm already living Written by Allyx Formalejo | July 13, 2026 Someone recently told me they thought they were experiencing arrival fallacy. I’d heard the term before. It describes the feeling of reaching…...
New MASAC iron guidelines reveal a ‘new normal’ for bleeding disorders
2+ week, 3+ day ago (607+ words) The standard numbers suggest I'm fine, but the new guidelines show I'm not Written by Jennifer Lynne | July 10, 2026 For most of my life, “tired” was the only word I had, and it was never enough. I’d say it to doctors…...
Standard hemophilia tool may miss joint damage in female patients
2+ week, 1+ day ago (549+ words) Study: Assessment relies entirely on healthy male reference data Written by Michela Luciano, PhD | July 10, 2026 The Haemophilia Joint Health Score (HJHS), a standard tool used to assess joint health in people with bleeding disorders, including hemophilia, may underestimate joint damage,…...
The bleeding disorders community reminds us we are not alone
2+ week, 4+ day ago (489+ words) Today, my wife and I try to pay their support and guidance forward Written by Joe MacDonald | July 9, 2026 My sons, Julian and Caeleb, were both diagnosed with hemophilia as babies. Although they’re 10 years apart, each diagnosis was overwhelming and affected…...
The bleeding disorders community eased the isolation of hemophilia
2+ week, 4+ day ago (271+ words) We found understanding, support, and a sense of belonging Written by Cazandra Campos-MacDonald | July 8, 2026 But there’s one thing my educator father didn’t teach me that I wish he had. My dad didn’t teach me to speak Spanish. My dad believed…...
Hemophilia A treatments may shape children’s immune responses
3+ week, 4+ day ago (650+ words) Study compares Hemlibra, factor VIII therapy in small pediatric group Written by Michela Luciano, PhD | June 30, 2026 In a small study, children with hemophilia A had distinct changes in certain immune cells and inflammatory signaling molecules compared with healthy children, and…...