Children, adolescents see Spinraza benefits in real-world study Written by Andrea Lobo | Oct. 26, 2026 Treatment with Spinraza (nusinersen) led to sustained improvements in motor function in children and adolescents with spinal muscular atrophy (SMA), according to a real-world study from Czechia…
The state govt has initiated steps to ensure lifelong access to life-saving medication for all eligible children suffering from spinal muscular atrophy (SMA), health minister K Muraleedharan told the assembly on Thursday.
Kerala health minister informed that the government had ordered a detailed investigation to examine the deaths and determine whether other patients who received the medication had experienced any adverse effects Kerala Health Minister K. Muraleedharan said in the assembly that there…
Replying to a submission, Minister says government is taking several steps through Kerala United Against Rare Diseases scheme to provide timely treatment and life-saving medicines to children affected by SMA Published - October 29, 2026 03:04 pm IST - Thiruvananthapuram The Kerala government has issued…
CHATTANOOGA, TN.- It’s time for the annual Chattanooga Fire Department’s Fill-the-Boot drive to support the Muscular Dystrophy Association. For more than 70 years, firefighters across the country have partnered with MDA to raise funds and awareness. CFD personnel will be out…
Givinostat (Duvyzat; ITF Therapeutics) in combination with corticosteroids delayed Duchenne muscular dystrophy (DMD) progression and demonstrated long-term safety and tolerability in ambulatory patients aged 6 and older, according to a study published in Annals of Clinical and Translational Neurology.1 The findings, which…
Why the research is interesting: The findings demonstrate that motor deficits in neurodevelopmental disorders can be associated with defects in specific brain circuits and that these circuits can retain a degree of plasticity later in life. This emphasizes the importance…
Interested in Cumberland Pharmaceuticals Inc.? Here are five stocks we like better. In the Phase II trial, the high-dose group showed improved left ventricular ejection fraction and reduced NT-proBNP versus placebo and natural-history controls, though the FDA has questioned whether…
CHATTANOOGA, Tenn. — It’s time for the annual Fill-the-Boot drive to support the Muscular Dystrophy Association (MDA). For more than 70 years, firefighters across the country have partnered with MDA to raise funds and awareness in the fight against neuromuscular diseases. The…
Published - October 26, 2026 01:54 pm IST - THIRUVANANTHAPURAM The Congress-led United Democratic Front (UDF) government in Keralam on Monday strongly defended the switch to a generic drug for patients with spinal muscular atrophy (SMA) and said it would try to further reduce the…
Duchenne and other muscular dystrophies and spinal muscular atrophy: gene therapies, new drugs and care.
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